Rising health awareness, increasing prevalence of various forms of mucopolysaccharidosis worldwide, continuous advances in ...
Ultragenyx Pharmaceutical RARE announced that the European Commission (EC) has expanded the eligible patient population for ...
In 2021, Gunner from Highley, Shropshire, was diagnosed with Mucopolysaccharidosis Type I Hurler Syndrome, which stops his body breaking down sugar. He was given one-to-two years to live without a ...